Sickle Cell Disease
4 stories
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healthCRISPR Cas12a Therapy Boosts Hemoglobin in Sickle Cell Disease
Phase 1-2 data show CRISPR gene editing normalizes hemoglobin and slashes vaso-occlusive events in severe sickle cell disease.
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healthNew Conditioning Regimen Boosts Sickle Cell Transplant Success
A novel stem cell transplant regimen for sickle cell disease shows 100% survival and low graft versus host disease rates in adolescents and adults.
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healthCRISPR Pioneers Win $3 Million for Revolutionary Sickle Cell Therapy
Two scientists awarded the Breakthrough Prize for developing the first CRISPR-based gene therapy, offering a functional cure for sickle cell disease and beta-thalassemia.
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healthStudy: Opioid Use, Not Race, Drives Bias in Sickle Cell Disease Notes
New research reveals clinician language in electronic health records shows bias linked to opioid use in sickle cell disease patients, surpassing race or chronic pain associations.