CRISPR
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healthGene Trade-Off: Rapid Growth Linked to Higher Cancer Risk in Vertebrates
Hebrew University scientists identify the vgll3 gene as a driver of early growth and late-life cancer in killifish, offering rare proof of antagonistic pleiotropy in vertebrates.
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healthRegeneron Leader: Europe's Clinical Trials at a Crossroads
Muriel O'Byrne of Regeneron discusses regulatory bottlenecks, genetic breakthroughs, and leadership in clinical trials.
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healthCRISPR Cas12a Therapy Boosts Hemoglobin in Sickle Cell Disease
Phase 1-2 data show CRISPR gene editing normalizes hemoglobin and slashes vaso-occlusive events in severe sickle cell disease.
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healthCRISPR Pioneers Win $3 Million for Revolutionary Sickle Cell Therapy
Two scientists awarded the Breakthrough Prize for developing the first CRISPR-based gene therapy, offering a functional cure for sickle cell disease and beta-thalassemia.
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healthGene Editing Breakthrough: New Therapy Shows Promise for Beta-Thalassemia
A novel gene editing approach successfully treats beta-thalassemia in a clinical trial, reactivating fetal hemoglobin and eliminating transfusion dependency.
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healthNanotech Revolutionizes Autoimmune Disease Treatment
Precision nanomedicine targets autoimmune disorders with reduced toxicity and enhanced immune modulation, offering a new era in therapeutic care.
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healthBC Teen Cured of Rare Genetic Disease Through Groundbreaking DNA Editing
A 19-year-old from British Columbia has been effectively cured of a life-threatening genetic disorder using advanced gene editing technology, offering hope for future treatments.
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healthUCLA Breakthrough: Gene Therapy Restores Cystic Fibrosis Function
UCLA researchers achieve gene therapy milestone, restoring full CFTR function in cystic fibrosis cells using non-viral nanoparticles.