CRISPR
-
healthRegeneron Leader: Europe's Clinical Trials at a Crossroads
Muriel O'Byrne of Regeneron discusses regulatory bottlenecks, genetic breakthroughs, and leadership in clinical trials.
-
healthCRISPR Cas12a Therapy Boosts Hemoglobin in Sickle Cell Disease
Phase 1-2 data show CRISPR gene editing normalizes hemoglobin and slashes vaso-occlusive events in severe sickle cell disease.
-
healthCRISPR Pioneers Win $3 Million for Revolutionary Sickle Cell Therapy
Two scientists awarded the Breakthrough Prize for developing the first CRISPR-based gene therapy, offering a functional cure for sickle cell disease and beta-thalassemia.
-
healthGene Editing Breakthrough: New Therapy Shows Promise for Beta-Thalassemia
A novel gene editing approach successfully treats beta-thalassemia in a clinical trial, reactivating fetal hemoglobin and eliminating transfusion dependency.
-
healthNanotech Revolutionizes Autoimmune Disease Treatment
Precision nanomedicine targets autoimmune disorders with reduced toxicity and enhanced immune modulation, offering a new era in therapeutic care.
-
healthBC Teen Cured of Rare Genetic Disease Through Groundbreaking DNA Editing
A 19-year-old from British Columbia has been effectively cured of a life-threatening genetic disorder using advanced gene editing technology, offering hope for future treatments.
-
healthUCLA Breakthrough: Gene Therapy Restores Cystic Fibrosis Function
UCLA researchers achieve gene therapy milestone, restoring full CFTR function in cystic fibrosis cells using non-viral nanoparticles.
-
healthScientists Uncover Brain's Defense Against Dementia
New research identifies the 'cellular hazmat team' that protects neurons from toxic protein buildup, offering hope for Alzheimer's and dementia treatments.