4 stories tagged #sickle cell disease

  1. CRISPR Cas12a Therapy Boosts Hemoglobin in Sickle Cell Disease
    health

    CRISPR Cas12a Therapy Boosts Hemoglobin in Sickle Cell Disease

    Phase 1-2 data show CRISPR gene editing normalizes hemoglobin and slashes vaso-occlusive events in severe sickle cell disease.

    last mo. 1 min read
  2. New Conditioning Regimen Boosts Sickle Cell Transplant Success
    health

    New Conditioning Regimen Boosts Sickle Cell Transplant Success

    A novel stem cell transplant regimen for sickle cell disease shows 100% survival and low graft versus host disease rates in adolescents and adults.

    last mo. 1 min read
  3. CRISPR Pioneers Win $3 Million for Revolutionary Sickle Cell Therapy
    health

    CRISPR Pioneers Win $3 Million for Revolutionary Sickle Cell Therapy

    Two scientists awarded the Breakthrough Prize for developing the first CRISPR-based gene therapy, offering a functional cure for sickle cell disease and beta-thalassemia.

    last mo. 2 min read
  4. Study: Opioid Use, Not Race, Drives Bias in Sickle Cell Disease Notes
    health

    Study: Opioid Use, Not Race, Drives Bias in Sickle Cell Disease Notes

    New research reveals clinician language in electronic health records shows bias linked to opioid use in sickle cell disease patients, surpassing race or chronic pain associations.

    last mo. 1 min read